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Allele-specific silencing therapy Gene therapy BAF Exon skipping Cell-penetrating peptide Microarray Expanded repeats Dominant centronuclear myopathy ITSN1 Mechano-transduction 3D co-culture Glucose Drisapersen Fibroblast Allele-specific silencing Flavonoid Neuromuscular junction Exon-skipping Duchenne muscular dystrophy Insulin Gene network analysis Endocytosis Gut microbiota Antisense morpholino HDMD/Dmd-null mice Migration CTG⋅CAGn repeat Laminographie Exondys 51 RNA interference CXCR4 Lamin A/C nuclei MT RNA/DNA Editing Muscle Actin Adhesion Eteplirsen DM1 myoblasts Glucocorticoid-induced muscle atrophy DMD CDNA synthesis Autophagosome Human artificial chromosomes Dynamin 2 DsDNA break repair LRP4 DNM2 Bile acid CXCL12 CMS Computer software Motor neuron Dystrophin MSCs CRISPR/Cas9 FoxO Fibrosis Acetylcholine receptor subunit epsilon Emerin ICU-acquired weakness Myotube Differentiation Immortalized dystrophic canine myoblast Folding-defective proteins Becker muscular dystrophy Human muscle stem/progenitor cells LTβR Conjugation Lymphotoxin-β-receptor Adeno-associated viral vector Skeletal muscle Mitochondrial ROS Human Developmental biology BMD Centronuclear myopathy Autophagy Fear response Mdx52 mice Canine X-linked muscular dystrophy in Japan CXMD J Coculture Gel electrophoresis Atrial cardiac defects FSHD Myogenesis Alternative splicing Mechanisms of disease Immortalisation Lamina-associated domain Cell biology Machine learning Myotonic dystrophy Clinical trial candidate screening Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS CFTR correctors Mdx KLF15 Antisense oligonucleotide Chromatin CLS